Scientists take major step toward Angelman Syndrome gene therapy

Scientists take major step toward Angelman Syndrome gene therapy

Babies born with a faulty maternal copy of the UBE3A gene will develop Angelman syndrome, a severe n...
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Pfizer Receives FDA Fast Track Designation for Duchenne Muscular Dystrophy Investigational Gene Therapy PF-06939926

Pfizer Receives FDA Fast Track Designation for Duchenne Muscular Dystrophy Investigational Gene Therapy PF-06939926

NEW YORK–(BUSINESS WIRE)–October 01, 2...
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Alzheimer’s: New gene may drive earliest brain changes

Alzheimer’s: New gene may drive earliest brain changes

A newly discovered Alzheimer’s gene may driv...
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Scientists identify gene that first slows, then accelerates, progression of ALS in mice

Scientists identify gene that first slows, then accelerates, progression of ALS in mice

Columbia scientists have provided new insights int...
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Parkinson’s disease linked to gene targeted by blue-green algae toxin

Parkinson’s disease linked to gene targeted by blue-green algae toxin

Scientists have discovered a possible link between...
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Percentage of African ancestry affects gene expression

Percentage of African ancestry affects gene expression

The percentage of African ancestry in a person&#82...
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Gene mutation in the chloride channel triggers hyperaldosteronism

Gene mutation in the chloride channel triggers hyperaldosteronism

Hyperaldosteronism is a disease primarily affectin...
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Gene editing enables researchers to correct mutation in muscle stem cells in DMD model

Gene editing enables researchers to correct mutation in muscle stem cells in DMD model

Duchenne muscular dystrophy (DMD) is a rare but de...
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Gene therapy helps functional recovery after stroke

Gene therapy helps functional recovery after stroke

A new gene therapy turns glial cells—abundant su...
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After 10-year search, scientists find second ‘short sleep’ gene

After 10-year search, scientists find second ‘short sleep’ gene

After a decade of searching, the UC San Francisco ...
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